Sometimes, in genetics, two wrongs do make a right. A research team has recently shown that two harmful genetic variants, ...

The human genome has to be carefully organized so it will fit inside of the nuclei of cells, while also remaining accessible ...

We know the genes, but not their functions—to resolve this long-standing bottleneck in microbial research, a joint research ...

No gene acts alone: interacting variants and protein partnerships can worsen, mask or even rescue disease risk, demanding ...

We know the genes, but not their functions.” To resolve this long-standing bottleneck in microbial research, a joint research ...

More than 9 out of 10 Alzheimer's cases could be driven by specific variations in a single gene and the protein it produces, ...

Explore RNA interference methods, comparing siRNA and shRNA for gene knockdown, their mechanisms, advantages, and ...

The company has started enrolling patients into a run-in period for the Phase III study, and plans to begin dosing later this ...

Multi-asset pipeline with significant targeted data readouts and milestones -- Two lead ophthalmic gene therapy programs in clinical trials ...

The firm at the JP Morgan Healthcare Conference additionally expects a regulatory decision on its gene therapy RGX-121 for Hunter syndrome next month.